Amicus Therapeutics presents additional data from Amigal Phase 2 extension study for Fabry disease

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Feb 11 2010

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Amicus Therapeutics (Nasdaq: FOLD) announced today additional positive preliminary data from its ongoing Phase 2 extension study of its investigational drug Amigal™ (migalastat HCl) for Fabry disease at the Lysosomal Disease Network WORLD Symposium in Miami, Florida. The Company also presented encouraging data from preclinical studies evaluating the combination of pharmacological chaperones and enzyme replacement therapy (ERT) for Fabry disease and Pompe disease as well as from preclinical studies examining the use of pharmacological chaperones for the treatment of Parkinson's disease.

SOURCE Amicus Therapeutics

Posted in: Drug Trial News | Medical Condition News

Tags: Arthralgia, Brain, Chaperones, Chromosome, Diarrhea, Enzyme, Fabry Disease, Headache, Neurodegeneration, Parkinson's Disease, Pompe Disease, Preclinical, Stroke, Therapeutics

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